Blog
Heart Care in Duchenne: Why Monitoring Starts Early
DMD cardiomyopathy is now the leading cause of death in Duchenne. Early heart monitoring and cardio-protective therapy are core to current standards of care.
Blog
Notes and updates
Shorter posts on DMD news, policy, and research. Useful context between long-form articles.
#access#adulthood#advocacy#basics#becker#cardiac#care#carriers#children#clinical-trials#cost#diagnosis#dmd#dystrophin#editorial#exon-skipping#families#gene-therapy#genetics#georgia#global#heart#history#inclusion#mental-health#meta#misinformation#monitoring#newborns#policy#rare-disease#research#safety#school#screening#standards#standards-of-care#steroids#symptoms#testing#transition#treatments
Blog
DMD Patient Advocacy History and Impact
Dmd patient advocacy history shows how families shaped research priorities, drug review, care standards, and access debates.
Blog
Health Misinformation Rare Disease Therapy Debates
Health misinformation rare disease debates can distort uncertainty, trust, access, and family decision-making around emerging therapies.
Blog
Newborn Screening for Duchenne: Pros and Limits
Newborn screening for Duchenne may support earlier care and counseling, but evidence, ethics, and treatment access remain unsettled.
Blog
Duchenne Treatment Access Georgia: What Happened
Duchenne treatment access in Georgia: how evidence, cost, protests, and misinformation collided in a rare disease care debate.
Blog
DMD Treatment Access by Country: Why It Varies
Dmd treatment access by country varies through regulators, payers, health technology assessment, pricing, and local budgets.
Blog
DMD Transition to Adulthood: Planning Ahead
Dmd transition to adulthood covers adult care, independence, assistive technology, education, work, and identity.
Blog
Mental Health Duchenne Muscular Dystrophy Guide
Mental health in Duchenne muscular dystrophy care: patients, parents, siblings, anxiety, depression, behavior, and caregiver strain.
Blog
School Accommodations Duchenne Families Can Discuss
School accommodations for Duchenne can cover access, fatigue, learning, emergency planning, mobility, and inclusion in everyday school life.
Blog
DMD Standards of Care: What Good Care Includes
Dmd standards of care include coordinated neuromuscular, heart, lung, rehab, bone, nutrition, and psychosocial support.
Blog
DMD Clinical Trial: A Family Reading Guide
Use this dmd clinical trial guide to understand phases, endpoints, eligibility, placebo, risks, and questions for a care team.
Blog
DMD Treatment Cost: Why Prices Are So High
Understand dmd treatment cost factors, including rare disease economics, manufacturing, evidence uncertainty, and payer decisions.
Blog
Gene Therapy Duchenne Muscular Dystrophy Update
Gene therapy for Duchenne muscular dystrophy, updated: micro-dystrophin, FDA approval, safety signals, and the unresolved questions ahead.
Blog
Exon Skipping Duchenne Therapies Explained
Exon skipping for Duchenne, explained: who may qualify, why approvals differ across jurisdictions, and why evidence debates continue.
Blog
Corticosteroids in Duchenne Muscular Dystrophy
Corticosteroids in Duchenne muscular dystrophy: evidence on benefits, side effects, and the treatment questions families can bring to clinicians.
_07.jpg?width=1200)
Blog
DMD Diagnosis: From Suspicion to Confirmation
Understand the dmd diagnosis pathway, from early symptoms and CK testing to genetic confirmation and specialist follow-up.
Blog
Early Signs of Duchenne Muscular Dystrophy
Early signs of Duchenne muscular dystrophy include delayed walking, frequent falls, calf enlargement, and when to ask a clinician about testing.
Blog
DMD Carrier Mother: What to Know
A dmd carrier mother may need genetic counseling, family testing, and cardiac follow-up. Learn the questions to raise with clinicians.
Blog
The Dystrophin Gene Explained Simply
This dystrophin gene explained guide covers what dystrophin does, how mutations disrupt muscle, and why results shape DMD care.
Blog
Duchenne vs Becker Muscular Dystrophy
Duchenne versus Becker muscular dystrophy in plain English: the shared gene, the different severity, and the diagnosis questions families ask.
Blog
What Is Duchenne Muscular Dystrophy?
What is Duchenne muscular dystrophy? Why it affects muscle, how symptoms appear, and what families can ask their care team next.
Blog
Welcome to DMD Awareness
Why this site exists, what we publish, and the editorial principles behind it.