Blog
Joining a Clinical Trial: What It Means for a Duchenne Family
Deciding whether a child joins a Duchenne clinical trial is hard. What participation involves, the hopes and burdens, questions to ask, and how families weigh it.
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#research
All articles and blog posts tagged #research.
Blog
Blog
Patient Registries and Natural History Studies in DMD
DMD patient registries: CINRG, Duchenne Registry, TREAT-NMD, MD STARnet. What they do, who can join, and why enrollment supports the whole community.
Blog
The DMD Research Pipeline: What's Beyond Approved Therapies
DMD research pipeline: CRISPR gene editing, next-generation gene therapy, exon skipping advances, anti-fibrotic approaches, and what families should know.
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DMD Clinical Trial: A Family Reading Guide
Use this dmd clinical trial guide to understand phases, endpoints, eligibility, placebo, risks, and questions for a care team.