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Gene Therapy Duchenne Muscular Dystrophy Update
Gene therapy for Duchenne muscular dystrophy, updated: micro-dystrophin, FDA approval, safety signals, and the unresolved questions ahead.
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#treatments
All articles and blog posts tagged #treatments.
Blog
Blog
Exon Skipping Duchenne Therapies Explained
Exon skipping for Duchenne, explained: who may qualify, why approvals differ across jurisdictions, and why evidence debates continue.
Blog
Corticosteroids in Duchenne Muscular Dystrophy
Corticosteroids in Duchenne muscular dystrophy: evidence on benefits, side effects, and the treatment questions families can bring to clinicians.